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Results for “United Kingdom”
Sponsor: AstraZeneca
Transthyretin Amyloidosis · ATTR-CM · ATTRv-PN · ATTR
United States, Canada, China, Germany, Spain +1 more
Sponsor: Novartis Pharmaceuticals
Scleroderma, Diffuse
United States, Argentina, Australia, Austria, Belgium +17 more
- A Phase 2 Study Evaluating Safety and Tolerability of RCT2100 (CFTR mRNA) in Healthy Participants and in Participants With CFActive Not Recruiting
Sponsor: ReCode Therapeutics
Cystic Fibrosis
United States, France, Netherlands, New Zealand, United Kingdom
- A Study of [177Lu]Lu-DOTA-TATE in Newly Diagnosed ES-SCLC Patients in Combination With Carboplatin, Etoposide and AtezolizumabActive Not Recruiting
Sponsor: Novartis Pharmaceuticals
Extensive Stage Small Cell Lung Cancer
United States, Austria, Canada, China, Czechia +7 more
- COMparison Between Anakinra and Tocilizumab in NORSE - "COMBAT-NORSE"Not Yet Recruiting
Sponsor: Yale University
New Onset Refractory Status Epilepticus · New-Onset Refractory Status Epilepticus · Febrile Infection-Related Epilepsy Syndrome (FIRES)
United States, Canada, France, Italy, South Korea +2 more
- A Study to Assess the Effectiveness and Safety of Pacritinib in Patients With VEXAS Syndrome (PAXIS)Active Not Recruiting
Sponsor: Swedish Orphan Biovitrum
VEXAS · VEXAS Syndrome
United States, Canada, France, Germany, Italy +3 more
- Phase 1/2 Clinical Trial of PR001 in Infants With Type 2 Gaucher Disease (PROVIDE)Active Not Recruiting
Sponsor: Prevail Therapeutics
Gaucher Disease, Type 2
United States, United Kingdom
Sponsor: Mid and South Essex NHS Foundation Trust
Osteomyelitis - Foot
United Kingdom
- A Study of Surovatamig (AZD0486) Plus Rituximab in Previously Untreated Follicular Lymphoma PatientsRecruiting
Sponsor: AstraZeneca
Untreated Follicular Lymphoma
United States, Australia, Belgium, Brazil, Canada +18 more
Sponsor: University of Ulster
Ileostomy - Stoma
United Kingdom
Sponsor: argenx
Spinal Muscular Atrophy (SMA)
United States, United Kingdom
Sponsor: Bayer
Chronic Kidney Disease · Proteinuria
United States, Argentina, Australia, Austria, Belgium +27 more
Sponsor: AstraZeneca
B-cell Acute Lymphoblastic Leukemia (B-ALL)
United States, Australia, Brazil, Canada, China +8 more
Sponsor: Bristol-Myers Squibb
Obstructive Hypertrophic Cardiomyopathy
United States, Austria, Czechia, France, Germany +4 more
- A Study to Identify Breast Cancer (IDBC)Recruiting
Sponsor: Syantra Inc.
Breast Cancer Female
Canada, South Korea, United Kingdom
Sponsor: Boehringer Ingelheim
Small Cell Lung Cancer (SCLC) · Extensive-stage Small Cell Lung Cancer (ES-SCLC)
United States, Argentina, Australia, Austria, Belgium +37 more
Sponsor: BeOne Medicines
Chronic Lymphocytic Leukemia
United States, Australia, Brazil, Canada, China +12 more
Sponsor: Novartis Pharmaceuticals
Asthma
Bulgaria, Colombia, Guatemala, Hungary, Poland +3 more
- Study to Evaluate the Efficacy and Safety of PF-07055480 / Giroctocogene Fitelparvovec Gene Therapy in Moderately Severe to Severe Hemophilia A AdultsActive Not Recruiting
Sponsor: Pfizer
Hemophilia A
United States, Australia, Brazil, Canada, France +11 more
- Study of AZD5305 as Monotherapy and in Combination With Anti-cancer Agents in Patients With Advanced Solid MalignanciesActive Not Recruiting
Sponsor: AstraZeneca
Ovarian Cancer · Breast Cancer · Pancreatic Cancer · Prostate Cancer
United States, Australia, Canada, China, Czechia +9 more
Sponsor: Richmond Research Institute
Healthy · Fatty Liver · MASLD · MASLD - Metabolic Dysfunction-Associated Steatotic Liver Disease
United Kingdom
Sponsor: Peptilogics
Prosthetic-joint Infection
United States, United Kingdom
- Open-Label Extension Study to Assess GLM101 in PMM2-CDG PatientsEnrolling By Invitation
Sponsor: Glycomine, Inc.
Pmm2-CDG · Phosphomannomutase 2 Deficiency
United States, Czechia, France, Germany, Italy +3 more
- A Study of Efficacy and Safety of Ianalumab in Previously Treated Patients With Warm Autoimmune Hemolytic AnemiaActive Not Recruiting
Sponsor: Novartis Pharmaceuticals
Warm Autoimmune Hemolytic Anemia (wAIHA)
United States, Argentina, Australia, China, France +11 more
- Global Open-Label Extension Study of Del-desiran for the Treatment of DM1Enrolling By Invitation
Sponsor: Avidity Biosciences, Inc.
Myotonic Dystrophy Type 1 · DM1 · Myotonic Dystrophy · Myotonia
United States, Canada, Denmark, France, Germany +5 more